• Tools and Technology for Advancing Rare Disease Research and Drug Development

    White Papers
    Nov. 21, 2019

    This white paper discusses virtual mapping of natural histories, the application of predictive modeling to better understand comorbidities and disease progressions as well as linkage to longitudinal real-world data sets. The goal is to improve diagnosis of patients, improve the design and conducting of trials, and enable development of more treatment options for people living with rare diseases.

    This white paper discusses virtual mapping of natural histories, the application of predictive modeling to better understand comorbidities and disease progressions as well as linkage to longitudinal real-world data sets. The goal is to improve diagnosis of patients, improve the design and conducting of trials, and enable development of more treatment options for people living with rare diseases.